Latest News About Pompe

Updated 2026-05-15 21:02

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Blog - Canadian Association of Pompe

Aro Biotherapeutics has launched a Phase 1b clinical trial for ABX1100, a substrate reduction therapy (SRT). This Pompe Empowerment Workshop welcomes patients and their family from Ontario or the Maritimes, for networking, learning and sharing. This Substrate Reduction Therapy drug could be the first pill taken by mouth to treat Pompe disease. The #Pies4Pompe Challenge is an awareness campaign hosted by Canadian Association of Pompe and driven by community and public participation. … One of a...

www.pompecanada.com

Pompe Disease News – Pompe Disease News

Get the latest news on Pompe disease, its causes, symptoms, diagnosis, and treatments. Hear patient and caregiver voices from our growing Pompe community.

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News

Spark Therapeutics Stops Its Pompe Program The IPA has been informed that Spark Therapeutics has realigned its portfolio and made the difficult decision to stop its... Author: IPA News July 13, 2024 Amicus Therapeutics Announces Approval and Launch of New Pompe Disease Therapy in the European Union Amicus Therapeutics announces that the European Commission (EC) has granted approval for Opfolda® (miglustat), an enzyme stabilizer of cipaglucosidase alfa, an...

worldpompe.org

News Archives

This Substrate Reduction Therapy drug could be the first pill taken by mouth to treat Pompe disease. This Substrate Reduction Therapy drug could be the first pill taken by mouth to treat Pompe disease. One of a handful of gene therapy companies with pipelines that include Pompe disease. Today AVROBIO announced a halt to their programs. Amicus Therapeutics, announces the approval of Opfolda (miglustat) capsules, an enzyme stabilizer of cipaglucosidase alfa, by the European Commission for the...

www.pompecanada.com

Pompe News

Many people receive the plethora of global news items through Google Alerts, Facebook and other Pompe websites, for example "Pompe Disease News". Posts here will be restricted to significant developme

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Discover the particulars of Pompe

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